Termina ya este #WORLDSymposia y a pesar de los🦠,ha sido muy interesante conocer las ultimas novedades en enf. #lisosomales . Y como siempre,buenos momentos rodeado de grandes profesionales y amig@s. Gracias Cristina,Laura y Jorge J Cebolla de Takeda_ES por vuestro apoyo y amabilidad
This week at the 19th Annual WORLDSymposium, we’re at Booth #100 ready to discuss the impact we're making in the lysosomal and rare disease space. Visit us to learn about the ways we’re hoping to make a difference for patients. #WORLDSymposia #RareDisease #GM1
#1fdsm #fabry #fabry disease #WORLDSymposia #fabry diseaseawareness #raredisease #worldsymposium2023 #fabry research
Today, I had the opportunity to present my poster at the 19th Annual WORLDSymposium and watch my mentor, Frederick Ashby, present as a Platform Speaker! WORLDSymposia
What a fantastic, dedicated, and kind group of researchers to work with to advance therapy for #freesialicacidstoragedisease ( #fsasd ) #worldsymposia
Salla Treatment And Research (STAR)
We had an inspiring time convening with the founding & prospective members of the Begin_NGS consortium at #WORLDSymposia . Thank you to all who accompany us in our journey to help end the diagnostic & therapeutic odysseys.
#EndTheDiagnosticOdyssey #genomics #raredisease
The clinical trial results for LYS-GM101 on #GM1gangliosidosis were disappointing, but provided important lessons moving forward in designing #clinicaltrials for this neurodegenerative pediatric disease.
Thank you Arunabha Ghosh for presenting the results at #worldsymposia
#WORLDSymposium 2023 was a fascinating collaborative experience sharing & discussing insights into #MPS a #rare #lysosomal storage disease
Roberto Giugliani #WORLDSymposia #conference #clinicalresearch #clinicaltrials #drug #pentosan #PPS #therapy #treatment #pharma $PAR
The @WORLDSymposium has released registration for 2024! Sign up now and get the early registration rates by January 5, 2024!Sign up here: worldsymposia.org/worldsymposium…
#WORLDSymposia #CareAboutRare #RareDisease
Dr. Neal Weinreb wants YOU 🫵 to join us in Orlando I for this morning’s breakfast symposium on #GaucherDisease ! The session begins in 15 minutes, so come fix a plate & grab your seat now! #WORLDSymposium2023 #WORLDSymposia
Join us in Orlando as we present data from our first-in-human clinical trial of MZE001 to treat Pompe Disease, and preclinical work supporting the program’s advancement at the 2023 WORLDSymposia 2023. Presentation details below. #WORLDSymposia businesswire.com/news/home/2023…
Thank you Rafael A. Badell-Grau, PhD for representing our lab at WORLDSymposia 2023. Also, a special acknowledgement goes out to National MPS Society and Cure Sanfilippo Fdn for your fellowship supports!
RDRP and MPS Society UK, here for those with rare diseases will be presenting work on the emotional impacts of Fabry disease during the #WORLDSymposia poster session today - Thursday 8th February. You'll find us at Kiosk 29, poster number 318. We look forward to seeing you there #research #rarediseases #fabry
Today at WORLDSymposia we presented positive data from our first-in-human clinical trial of MZE001 to treat Pompe Disease - supporting advancement into our Phase 2 clinical trial in 2023. Details here: businesswire.com/news/home/2023…
Aaaand that’s a wrap. The sixth of CHOC / CHOC Docs platform presentations at the 2024 #worldsymposia is finished.
Also completed a commentary re: reliance of #raredisease tx on industry. Shareholder value is NOT aligned w interests of pts and their families
A full house at #WORLDSymposia to discuss innovations in lysosomal storage disorders like NPC. Thank you to Dr. Caroline Hastings for her oral presentation on our global Phase 3 study TransportNPC. It’s been a busy week!
$CYTH #NiemannPick #LysosomalDisease
It’s time to talk about CRISPRCas9 and MPS IVA. Here we go! 🇨🇴🇺🇸IEIM-PUJ Facultad Ciencias Pontificia Universidad Javeriana WORLDSymposia #GenomeEditing #CRISPR #LysosomalDiseases
