Orphan drugs are a lifeline for individuals with rare diseases, providing hope and improved quality of life. Their development and availability have transformed the landscape of healthcare. #LucyScientificInc $LSDI #OrphanDrugs #RareDiseases
It’s day 2 of the #orphandrugcongress where Alex Morrison, Benedicta Marshall-Andrew, and Samantha Wiseman, are using this invaluable opportunity to discuss, network and gain insights into innovative ideas in the fields of #orphandrugs and #rarediseases . #research #clinicaltrials
We have added a Publications menu on our website to share our published research. (And we have included a #preprint section too! )
miramoonpharma.com/index.php/publ…
#DrugDevelopment #SmallMolecules #RareDiseases #OrphanDrugs #OpenAccess
📷 NAnA today at the World Orphan Drug Congress Europe! Talking about #raredisease and #orphanmedicines !
@Orphan_Drugs
#WODC #Eurordis #uniamo #orphandrugs #scicomm #leucemie #AML
The start of a new week! 🌟
On Wednesday we'll be back in #Stockholm to present Redeye AB's special #OrphanDrugs event!
We'll take the stage at 13:30 CET and elaborate on our project for the #raredisease #Erythromelalgia !
redeye.se/events/870532/…
#PILA #Investment #Lifescience
OKYO Pharma Receives FDA Approval of IND for OK-101 in Neuropathic Corneal Pain (NCP). NCP is a major unmet medical need and listed as an Orphan disease.
$OKYO #neuropathiccornealpain #NCP #orphan drugs #orphan
okyopharma.com/okyo-pharma-re…
Missed our recent #orphandrugs #webinar ? Fear not.
Review the companies, drugs and therapy areas fuelling growth of the #pharma market and the impact of the #InflationReductionAct on orphan drug development.
On-demand version: bit.ly/3ZKCaua
Spannende Perspektiven heute auf der #NAKSE 2023.
Mein Beitrag zu #OrphanDrugs :
Zielgerichtetere Förderung und bessere Evidenz sind der Schlüssel für eine nachhaltige Versorgung von Menschen mit #SeltenenErkrankungen mit guten Therapien.
Allianz Chronischer Seltener Erkrankungen e.V.
If you are at #WODC2023 this week, be sure to connect with Tom Murtagh at the meeting, or reach out to us at [email protected] to learn more about how we can provide guidance in rare disease and gene therapy.
#cellandgenetherapy #orphandrugs #WorldOrphanDrugUSA
Today at NORD Summit in Washington D.C., our CEO, Stephen Uden, M.D., joins industry leaders to discuss the present and future of #rarediseases and #orphandrugs . Learn more about #NORDSummit : nordsummit.org/agenda/
Hear from Rachel Smith, Head of Rare Disease at Parexel, during the World Orphan Drug Congress in Boston this week!
parexel.com/about-us/event… #WODC #WODC 24 #raredisease #orphandrugs
Delighted that MDX-124 has received #EMA #Orphan Medicinal Product positive opinion for #pancreaticcancer driven by data showing inhibition of tumour growth and improved survival, and powerful synergy with standard of care treatments #rarediseaseday2023 #orphandrugs #oncology
Our Co-Founder & Executive Chairman, Martin Mackay, Ph.D., joins a panel NORD Summit today, 1:40pm ET, discussing orphan product investment now and in the years ahead. Learn more about #NORDSummit : nordsummit.org/agenda/ #RareDiseases #OrphanDrugs #biotechinvesting
SKC is excited to announce that we will be attending the World Orphan Drug Congress USA 2024 World Orphan Drug Congress USA, the most important and comprehensive event for the #RareDisease industry. Get more information on eu1.hubs.ly/H08jgJV0 #OrphanDrugs #MarketAccess #ATMPs #GeneTherapies
Second Panel with, among others, D'aria Jullowska, Scientific Coordinator of the European Joint Programme on #RareDiseases , and Avril Daly, President of EURORDIS-Rare Diseases Europe!
#WODC World Orphan Drug Congress EJP RD - European Joint Programme on Rare Diseases
#uniamo #scicomm #orphandrugs
My daughter with no treatment options joined a #drugtrial 3 years ago. #FDA has changed its requirement many times in the last few years for rare disease making it harder to approval #OrphanDrugs like AT-007. We just found out she was on placebo for 18 months. We now get to…
We are 6 months away from this year's #WODC 2024! 💫
This year is set to be our best one yet with over 2000+ attendees, 250+ speakers and 130+ exhibitors!
🎟️Register now to save 70% off on our tickets: buff.ly/3t7msim
#WODC #OrphanDrugs #RareDisease #OrphanDrugAdvocate
Tag der #SeltenenErkrankungen : Betroffene wollen sensibilisieren. Hoffnung gibt: ein Drittel der Medikamente, die in den vergangenen fünf Jahren auf den Markt kamen, sind #OrphanDrugs . vfa Pharma VCI #rarediseaseday Bild: Canva/Dall-E
🧬💊 #OrphanDrugs are developed specifically to treat #RareDiseases , offering hope and solutions to patients and families often overlooked by mainstream #pharmaceutical development.
Get access to cutting-edge information on the orphan drugs market at bit.ly/48FfboH
